Studien
Laufende Studien – Kooperation LMU
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Wertigkeit einer Gruppe von Biomarkern in der Differentialdiagnose von Kindern mit einer ersten demyelinisierenden Erkrankung des ZNS. Multicenter
Multiple Sklerose
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2012
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laufend
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neun
 
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Connect (109 MS306) Open-Label, Randomized, Multicenter, Multiple-Dose,Active-Controlled, Parallel-Group, Efficacy and Safety Study of BG00012 in Children
Multiple Sklerose
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2016
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laufend
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3
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neu
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NCT 2013-002318-11 EudraCT Number: 2013-002318-11
 
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SNT-III-012 - A Phase III Double blind, Randomized, Placebo Controlled Study assessing the Efficacy, Safety and Tolerability of Idebenone in Patients with Duchenne Muscular Dystrophy Receiving Glucocorticoid Steroids
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2016
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laufend
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3n
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neu
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DMD/EudraCT Nr.: 2016-000602-10
 
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DSC/14/2357/48 - Givinostat Randomised, double blind, placebo controlled, multicentre study to evaluate the efficacy and safety of givinostat in ambulant patients with Duchenne Muscular Dystrophy
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2018
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laufend
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3
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neu
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DMD/EudraCT Nr.: 2016-000401-36
 
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ATX-MTM-009 INCEPTUS - A Prospective, Non-Interventional Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects Aged 3 Years and Younger
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2016
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laufend
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natural history
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neu
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MTM/EudraCT Nr.: 2015-003769-27
 
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ATX-MTM-002 ASPIRO A Phase 1/2, Randomized, Open-Label, Ascending-Dose, Delayed-Treatment Concurrent Control Clinical Study to Evaluate the Safety and Preliminary Efficacy of AT132, an AAV8-Delivered Gene
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2018
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laufend
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1–3
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neu
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MTM/EudraCT Nr.: 2017-000876-27
 
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HINE (ISIS 396443-CS11) An Open-Label Extension Study for Patients With Spinal Muscular Atrophy Who Previously Participated in Investigational Studies of ISIS 396443
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2018
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laufend
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OLE
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neu
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SMA/EudraCT Nr.: 2015-001870-16
 
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CAT-1004-304: POLARIS DMD single global Phase 3 trial called POLARIS DMD in Duchenne to evaluate the efficacy and safety of edasalonexent
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2018
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laufend
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3
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neu
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NCT 03703882
 
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A Randomized, Active-Controlled, Open-Label, Flexible-Dose Study to Assess the Safety
and Tolerability of Topiramate as Monotherapy Compared With Levetiracetam as
Monotherapy in Pediatric Subjects With New or Recent-Onset Epilepsy
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2018
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3
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neu
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moma – modules on migraine activity
Strukturierte multimodale Frühintervention für Kinder mit Migräne im Alter von 6-11 Jahren
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2018
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2021
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neu
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Deutsches FASD KOMPETENZZENTRUM Bayern
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2018
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2021
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Ethikvotum